Mar 6, 2024 · An experimental treatment, NTLA-2002, resulted in a 95% drop in the number of monthly angioedema attacks among all study participants with hereditary angioedema.

Apr 11, 2024 · The life expectancy of patients with systemic mastocytosis (SM), when considered as a group, is shorter than that of the general population, with most

Antineutrophil cytoplasmic antibody (ANCA)-associated vasculitis (AAV) is a heterogeneous group of rare autoimmune diseases in which ANCA target and activate neutrophils. These, in turn, …

Are you a health care provider looking for information on immunoglobulin G4-related disease (IgG4-RD) signs and symptoms? Read more here.

Nov 25, 2024 · Inebilizumab therapy is associated with reduced disease flares and an increased likelihood of 1-year flare-free complete remission of IgG4-RD.

Systemic sclerosis (SSc) is a rare, autoimmune connective tissue disease that is characterized by chronic inflammation, vasculopathy, and excessive

Rare Disease News is the premier online resource for the latest rare disease news, perspectives and information.

Myasthenia gravis (MG) is a rare autoimmune disease in which the body attacks components of the neuromuscular junction (NMJ), causing weakness of voluntary skeletal muscles and …

Myelodysplastic syndromes (MDS) are a heterogenous group of hematological neoplasms characterized by a clonal disorder of hematopoietic stem cells that causes ineffective …

Antineutrophil cytoplasmic antibody (ANCA)-associated vasculitis (AAV) is a group of 3 diseases: granulomatosis with polyangiitis (GPA), eosinophilic granulomatosis with polyangiitis (EGPA), …