Entrada plans to initiate clinical testing of ENTR-601-44 in Duchenne MD patients amenable to exon 44 skipping later this year.
Caregivers of people with Duchenne muscular dystrophy may play an important role in the prevention and management of fat ...
Columnist Betty Vertin has learned that as a parent, she's finding the years with all her children, including those with DMD, too short.
The Muscular Dystrophy Association (MDA) is honoring a longtime researcher and an LGMD patient advocate with its 2025 Legacy ...
The U.S. Food and Drug Administration (FDA) has granted fast track designation to DYNE-101, a treatment candidate for myotonic dystrophy type 1 (DM1) — in which disease symptoms begin during adulthood ...
Top-line Phase 3 trial data show ambulatory boys with Duchenne continued with motor improvements two years after a single ...
Columnist Shalom Lim is working with Julia Cameron's popular book "The Artist's Way" as a route to develop his creative self, ...
Columnist Robin Stemple has to make yet another adjustment due to FSHD, after a fall left him feeling "like an upside-down ...
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