From February 12, all newborn babies will be offered screening for spinal muscular atrophy (SMA), a rare progressive neuromuscular disease. SMA will be one of more than 20 other rare disorders ...

Dysferlin-deficient muscular dystrophy is a devastating and untreatable disease. Using Cas9, the authors restored dysferlin in muscle stem cells from patients ex vivo and show proof-of-concept for ...

Biogen has announced that the European Medicines Agency (EMA) and US Food and Drug Administration (FDA) have started ...

A medical professional has gone viral on TikTok after discussing a health condition people need to know more about, as it can ...

From February 12, all newborn babies will be offered screening for spinal muscular atrophy (SMA), a rare progressive neuromuscular disease. SMA will be one of more than 20 other rare disorders ...

Exercise improves sleep quality and helps treat sleep disorders by regulating circadian rhythms, reducing stress, and ...

Klotho Neurosciences, Inc. (NASDAQ:KLTO – Get Free Report)’s stock price dropped 4.7% on Thursday . The stock traded as low as $0.37 and last traded at $0.40. Approximately 63,797 shares changed hands ...

Watching an older loved one's mind fade is often a slow, challenging experience for everyone involved. However, sometimes the memory loss can happen fast, leaving little time for answers.

Hyperkalemia is when you have very high levels of potassium and it comes on suddenly. If it comes on without warning, and is ...

UCB, a global biopharmaceutical company, today announced the CHMP (Committee for Medicinal Products for Human Use) has issued a positive opinion for the self-administration of RYSTIGGO® ...

The Wolfson Centre for Inherited Neuromuscular Disease, The Robert Jones and Agnes Hunt Orthopaedic and District Hospital NHS Trust, Oswestry, Shropshire, SY10 7AG, UK; ros.quinlivan{at}rjah.nhs.uk ...

Top-line Phase 3 trial data show ambulatory boys with Duchenne continued with motor improvements two years after a single ...