Proteins form the structural and functional backbone of the cell, and any perturbation in their synthesis can disrupt normal ...

A new study from Weill Cornell Medicine provides insights into how cells maintain the tiny end caps of chromosomes as they ...

Amyotrophic lateral sclerosis (ALS) is a relatively rare but very serious disease of the nervous system. A cure is not yet ...

As the field of proteomics continues to advance, scientists are using new methods to answer longstanding questions about rare ...

In a study published in the Journal of the American Chemical Society, scientists explore how a brain protein called tau changes its behavior when a small chemical group called a phosphate attaches to ...

CSL Behring Austria today announced that the first haemophilia B patient in Austria was treated with the gene therapy HEMGENIX® (etranacogene dezaparvovec) at the Comprehensive Care Center of the ...

For hemophilia B patients, frequent bleeding can easily lead to damage to joint structure and function ... an inherited bleeding disorder caused by the deficiency of the clotting protein factor IX ...

Protein structure predictions are bioinformatic analyses that produce predicted protein structures automatically using the protein amino acid sequence. Protein structures are important because ...

Discover how an emerging technology called tRNA therapy could become the next big thing in genetic disease treatment.

The expression of green fluorescence protein (GFP) following transduction with rAAV5-CMV ... to neutralization than AAV5 which has already been utilized to treat hemophilia B. The clinical samples ...