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An international research team has identified a new protein that specifically transports enzymes into peroxisomes. Its mode ...
Munich news, health insurance, technology, jobs and other topics for expatriates. The Eye Newspapers covers daily news and offers services for foreigners.
Sangamo Therapeutics Inc. (NASDAQ:SGMO) is one of the best penny stocks under $1 to buy now. On June 24, Sangamo Therapeutics ...
A study evaluating a pioneering lentivirus (LV)-mediated gene therapy trial for classical Fabry disease showed promising ...
The global Enzyme Replacement Therapy (ERT) market is poised for significant expansion, projected to reach USD 21.62 billion ...
Ascendis’ likely approval of TransCon CNP for achondroplasia poses a major threat to BioMarin’s best-selling drug. Read why I ...
The FDA has accepted for Priority Review the BLA for tividenofusp alfa for the treatment of Hunter syndrome, also known as MPS II.
By Distribution channel Hospital & Clinics Pharmacies Retail Pharmacies Online Pharmacies Others ...
A little 4 year old girl named Skylar is being treated right now at Primary Children’s Hospital for a rare, progressive and ...
Scientists have successfully restored hearing in animal models of ENPP1 deficiency, a genetic disease in which individuals ...
Enzyme-replacement therapy with recombinant human GAA (rhGAA) has been a standard treatment for Pompe's disease since it was approved in 2006, they noted.