Phase 3 Aspire study enrollment on track to complete in 2025 Aurora study to evaluate GTX-102 in other Angelman syndrome genotypes and ages expected to initiate later this year NOVATO, Calif ...

Investing.com -- Ultragenyx Pharmaceutical Inc. (NASDAQ:RARE) stock gained 2.2% premarket after the company announced that its experimental treatment for Angelman syndrome received Breakthrough ...

First Patient Dosed In Phase 3 REVEAL Study Of ION582 For Angelman Syndrome. A scientist in a laboratory making a breakthrough discovery in biotechnology.

Angelman syndrome is a lifelong neurodevelopmental disorder that causes cognitive impairment, motor impairment, balance issues and debilitating seizures.

The Hometown Foundation is hosting a car show for Angelman syndrome in Cheshire.

Ionis Pharmaceuticals, Inc. (NASDAQ:IONS) is among the 11 Best Genomics Stocks to Buy According to Hedge Funds. The initial participant in the pivotal Phase 3 REVEAL trial, which is assessing ION582 ...

Ultragenyx Pharmaceuticals' GTX-102 earns FDA Breakthrough status after early data shows sustained progress in Angelman syndrome patients.

In a conversation with People magazine in 2024, Colin Farrell opened up for the first time about his son's rare condition: Angelman syndrome. Just before his son James’ 21st birthday, the actor ...

BRANFORD, Conn. (WTNH) — A portion of Interstate 95 North has heavy congestion Monday following a double rollover crash, according to state police. The multi-vehicle crash was reported in the ...

A woman has shared her dismay after being compared to a famous English football player - but some YouTube viewers believe this isn't her only celebrity lookalike ...

A woman has been unable to sleep after night after being compared to English footballer Cole Palmer - but people believe she has another celebrity lookalike out there ...