Muscular Dystrophy News17h
Phase 1/2 trial of exon 44 skipping therapy for DMD cleared in UK
Entrada plans to initiate clinical testing of ENTR-601-44 in Duchenne MD patients amenable to exon 44 skipping later this year.
Muscular Dystrophy News1d
A caregiver’s guide to FES and DMD
Caregivers of people with Duchenne muscular dystrophy may play an important role in the prevention and management of fat ...
Muscular Dystrophy News4d
To a parent, the years always seem too short
Columnist Betty Vertin has learned that as a parent, she's finding the years with all her children, including those with DMD, too short.
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MDA honors researcher, patient advocate with 2025 Legacy Awards
The Muscular Dystrophy Association (MDA) is honoring a longtime researcher and an LGMD patient advocate with its 2025 Legacy ...
Muscular Dystrophy News6d
Boys with DMD given Elevidys 2 years ago still showing motor gains
Top-line Phase 3 trial data show ambulatory boys with Duchenne continued with motor improvements two years after a single ...
Muscular Dystrophy News6d
How a Singapore ‘Artist’s Way’ program is rekindling my creativity
Columnist Shalom Lim is working with Julia Cameron's popular book "The Artist's Way" as a route to develop his creative self, ...
Muscular Dystrophy News6d
Another fall left me feeling like an upside-down turtle
Columnist Robin Stemple has to make yet another adjustment due to FSHD, after a fall left him feeling "like an upside-down ...