Discover the current pipeline candidates advancing through the clinic for the treatment of sickle cell disease.

Gabriella Ngang, of Farmington Hills, is one of three in Michigan to take part in a clinical trial of a new sickle cell disease gene-editing therapy.

Gene therapy for sickle cell disease may help improve a major contributing factor to stroke risk in patients, reports a new study from St. Jude Children's Research Hospital. Many people with ...

Gene therapy for sickle cell disease may help improve a major contributing factor to stroke risk in patients, reports a new study from St. Jude Children's Research Hospital.

States representing about 84% of Medicaid beneficiaries are participating in an initiative that enables the U.S. government ...

Scientists at St. Jude Children’s Research Hospital found that patients with sickle cell disease who received gene therapy experienced a return to normal blood flow in the brain.

CMS has reached agreements with drug manufacturers to provide gene therapies to treat sickle cell disease to Medicaid recipients under a new outcomes-based model. A total of 33 states, including the ...

Controlling the activity of specific genes in the laboratory through the editing of their epigenetic marks is now a reality ...

Vertex Pharmaceuticals may have narrowed its focus this year, but the biopharma’s decision to stick with its remaining islet cell therapy ...