The mum and dad of a baby with a genetic disease so rare it has no name have vowed to keep fighting for him after the ...

In a novel theory, scientists at Arizona State University's Biodesign Institute propose a unifying explanation for the ...

In two new papers, researchers from The Jackson Laboratory (JAX) report the successful use of two approaches -- gene therapy ...

UMD researchers have discovered key mechanisms in gene regulation that could improve the design of RNA-based medicines.