A study evaluating a pioneering lentivirus (LV)-mediated gene therapy trial for classical Fabry disease showed promising ...

What would you do to save your child? This mom is fighting to fund a cure for her daughter's terminal illness.

Sangamo Therapeutics Inc. (NASDAQ:SGMO) is one of the best penny stocks under $1 to buy now. On June 24, Sangamo Therapeutics ...

The global Enzyme Replacement Therapy (ERT) market is poised for significant expansion, projected to reach USD 21.62 billion ...

Hypophosphatasia is a relatively common skeletal disease that primarily affects bone and tooth strength. In the third ...

The Princess Royal officially opened Insmed’s new research and development facilities at Babraham Research Campus – and ...

Munich news, health insurance, technology, jobs and other topics for expatriates. The Eye Newspapers covers daily news and offers services for foreigners.

Over 5 years of treatment in hemophilia B patients, gene therapy research shows sustained factor IX activity and safety.

Starting on August 1st, the Wisconsin newborn screening program will be adding two genetic disorders X-ALD and MPS type 1 to ...

Three critically ill patients treated with procizumab experience a full reversal of cardiogenic shock in 48 hours.

Overview of Skeletal Dysplasia MarketThe Global Skeletal Dysplasia Market is valued at USD 3.42 Billion in 2024 and is ...

University of Geneva researchers led a collaboration for testing different size-exclusion chromatography columns to compare ...