Amyotrophic lateral sclerosis (ALS) is a fatal neurodegenerative disease that causes progressive muscle weakness. A research ...

Eight children were born with DNA from three people to prevent a deadly genetic disease.

Scientists at Princeton and the Simons Foundation have identified four biologically distinct subtypes of autism, using data ...

EMA’s CHMP issued an opinion not to recommend Elevidys™ (delandistrogene moxeparvovec) for the treatment of ambulatory individuals with Duchenne muscular dystrophy (DMD) Roche will continue its ...

Australian researchers are using peptides isolated from spider venom to develop treatments for a range of neurological and ...

Adrian R. Krainer has been awarded the 2025 Heinrich Wieland Prize for his pioneering RNA research that led to the ...