Cyclists led by Charlie Nuck will arrive in Bar Harbor Saturday to raise awareness and funds for the rare neurogenetic ...

That’s exactly what Charlie Nuck and Todd Downey, both from Ohio, have done. After biking more than 4,200 miles from Anacortes, Washington, the pair arrived in Bar Harbor, completing a two-month trek ...

Maine (WABI) - After 61 days and approximately 4,200 miles, two men have made it to Maine to wrap up an epic journey. At the ...

Investing.com -- Ultragenyx Pharmaceutical Inc. (NASDAQ: RARE) stock gained 2.2% premarket after the company announced that its experimental treatment for Angelman syndrome received Breakthrough ...

Angelman syndrome is a lifelong neurodevelopmental disorder that causes cognitive impairment, motor impairment, balance issues and debilitating seizures.

On June 27, Ultragenyx Pharmaceutical announced that the US FDA granted Breakthrough Therapy Designation for GTX-102 (apazunersen) as a treatment for Angelman syndrome.

Investing.com -- Ultragenyx Pharmaceutical (TADAWUL: 2070) Inc. (NASDAQ: RARE) stock gained 2.2% premarket after the company announced that its experimental treatment for Angelman syndrome received ...

The Hometown Foundation is hosting a car show for Angelman syndrome in Cheshire.