NOVATO, Calif., June 27, 2025 (GLOBE NEWSWIRE) -- Ultragenyx Pharmaceutical Inc. (NASDAQ: RARE), today announced that it has ...

Phase 3 Aspire study enrollment on track to complete in 2025 Aurora study to evaluate GTX-102 in other Angelman syndrome genotypes and ages expected to initiate later this year NOVATO, Calif., June 27 ...

Angelman syndrome is a rare condition that causes problems with growth and development. It’s caused by a genetic mutation (a change in your genes) that affects the nervous system. It’s named ...

More information: Jacqueline Fátima Martins de Almeida et al, Molecular aspects of Angelman Syndrome: Defining the new path forward, Biomolecules and Biomedicine (2025). DOI: 10.17305/bb.2025.11724 ...

According to DelveInsight's estimates, the Angelman syndrome market size in the 7MM is expected to show positive growth during the forecast period (2025–2034), primarily driven by the increasing ...

LAS VEGAS, June 2, 2025 /PRNewswire/ -- Angelman syndrome is a rare neurogenetic disorder affecting approximately 1 in 15,000 live births or 500,000 people globally.

The article in Genomic Psychiatry titled "Prader-Willi syndrome: Genetics, clinical symptoms, and model systems," is freely available via Open Access on 20 May 2025 in Genomic Psychiatry at the ...

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Angelman syndrome is a rare genetic disorder that mainly affects the nervous system and causes developmental delays, speech difficulties, and movement problems. The condition has recently gained ...

Actor Colin Farrell has opened up about the difficult decision to move his son James, who has Angelman syndrome, into a long-term care facility. The Oscar-nominated star of The Banshees of ...

Angelman syndrome explained as Colin Farrell opens up about son's rare condition Doctors initially thought Colin Farrell's son, James, had cerebral palsy before he was diagnosed with the rare ...

Actor Colin Farrell has opened up about the difficult decision to move his son James, who has Angelman syndrome, into a long-term care facility. The Oscar-nominated star of The Banshees of Inisherin, ...