STAT1d
At meeting on guardrails for gene editing of human embryos, some call for a dead end
At meeting on human embryo editing, CRISPR pioneer says science is a long way from knowing if germline DNA can be safely ...
Good News Network5d
Groundbreaking Gene Therapy Cures 21-year-old of His Sickle Cell Anemia: ‘I’m not in pain anymore’
Sebastien Beauzile, 21, is the first New Yorker to have received the breakthrough Lyfgenia treatment, according to the New ...
Hosted on MSN1mon
New sickle cell treatment cures disease at lower cost than gene therapies
Meanwhile, sickle cell gene therapies Casgevy and Lyfgenia cost $2.2 million and $3.1 million, respectively. More than half of people in the U.S. with sickle cell disease are enrolled in Medicaid ...
Scientists identify potential new genetic target for sickle cell disease treatment
Scientists from Johns Hopkins Medicine and eight other institutions in the United States, Africa and Europe say they have ...
Sickle cell anemia patient reunites with Long Island doctors whose gene therapy treatments made him symptom-free
Sebastien Beauzile became the first person in NY to be made symptom-free after undergoing a new type of gene therapy.
pharmaphorum1d
Sickle cell gene therapy Casgevy finally cleared for NHS use
Vertex Pharma's £1.65 million ($2.05 million) gene-editing therapy for sickle cell disease (SCD), Casgevy, has been given the green light for use by the NHS in England under a managed access ...
WRAL1y
FDA approves two gene therapies for sickle cell, bringing hope to thousands with the disease
(CNN) — The US Food and Drug Administration on Friday approved two gene-based treatments for sickle cell disease, including the first therapy that uses the gene-editing technique CRISPR ...
High-cost sickle cell gene therapies push insurers and Medicaid programs to find new payment models
Deshawn "DJ" Chow is one of just over 100 sickle cell patients who have undergone treatment with new gene therapies. CVS Health CEO David Joyner said private insurers and employer-sponsored health ...
PBS8y
A Mutation Story:
A gene known as HbS was the center of a medical and evolutionary detective story that began in the middle 1940s in Africa. Doctors noticed that patients who had sickle cell anemia, a serious ...
TribLIVE.com1y
2 gene therapies for sickle cell disease approved in U.S.
Associated Press Friday, Dec. 8, 2023 12:50 p.m. | Friday, Dec. 8, 2023 12:50 p.m. Regulators on Friday approved two new gene therapies for sickle cell disease that doctors hope can cure the ...
pharmaphorum1y
ICER backs sickle cell gene therapies at one-off cost of $2m
The influential Institute for Clinical and Economic Review (ICER) in the US has issued draft guidance suggesting that new gene therapies for sickle cell disease (SCD) from Vertex Pharma and ...