Sebastien Beauzile, 21, is the first New Yorker to have received the breakthrough Lyfgenia treatment, according to the New ...

Scientists from Johns Hopkins Medicine and eight other institutions in the United States, Africa and Europe say they have ...

A sickle cell gene therapy treatment has allowed a Long Island man to turn a chapter in his life, with doctors declaring him ...

Development of a stem cell therapy for sickle cell disease from Vertex and development partner CRISPR therapeutics can go ahead, after the FDA lifted a hold on a review. The companies had applied ...

Medical history has recently been made in a New York City hospital. This month, 21-year-old Sebastien Beauzile became the ...

In 2008, Orkin, Sankaran, and colleagues achieved their vision by identifying a new therapeutic target for sickle cell disease. In December 2023, through the development efforts of CRISPR ...

Sickle cell anemia is an inherited hemolytic anemia with abnormal hemoglobin protein that causes red blood cells to be rigid and clog circulation through small blood vessels. Anemia of chronic ...

For example, in the treatment of monogenic diseases like cystic fibrosis, sickle cell disease, and osteogenesis imperfecta, CRISPR technologies have shown promise in correcting disease-causing ...

Shares of biotechnology stocks such as Recursion Pharmaceuticals (NASDAQ: RXRX), Summit Therapeutics (NASDAQ: SMMT), and CRISPR Therapeutics ... blindness, sickle cell anemia, and child leukemia ...

CRISPR is a technology that can be used to edit genes and, as such, will likely change the world. The essence of CRISPR is simple: it’s a way of finding a specific bit of DNA inside a cell.