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Scientists have corrected gene mutations in mice causing an ultra-rare disease by editing DNA directly in the brain with a ...
Scientists have corrected gene mutations in mice causing an ultra-rare disease by editing DNA directly in the brain with a single injection, a feat with profound implications for patients with ...
Prime editing corrects the most common genetic mutations that cause alternating hemiplegia of childhood (AHC), a rare and ...
Early research shows replacing brain immune cells slows a rare brain disease, with potential implications for treating ...
By the time they are a few months old, infants born with alternating hemiplegia of childhood (AHC) begin experiencing ...
Scientists have corrected gene mutations in mice causing an ultra-rare disease by editing DNA directly in the brain with a ...
At 8 years old, Axi Mok was diagnosed with the rare disease Hashimoto’s encephalopathy, a rare brain disorder that caused her ...