Dysferlin-deficient muscular dystrophy is a devastating and untreatable disease. Using Cas9, the authors restored dysferlin in muscle stem cells from patients ex vivo and show proof-of-concept for ...

It's a rare autoimmune neuromuscular disease that causes weakness and fatigue ... The key is to recognize the signs and symptoms and get the right diagnosis early on. Helping me to break it ...

The Neuromuscular Disease Center has a long history of providing excellent ... and double vision along with other possible symptoms. Our clinic provides expert diagnostic services and state-of-the-art ...

The symptoms are of a slowly progressive numbness and tingling that usually starts in the feet, but later spreads to the legs and hands. The patients also complain of some weakness, again usually ...