Sebastien Beauzile, 21, is the first New Yorker to have received the breakthrough Lyfgenia treatment, according to the New ...

Sebastien Beauzile is the first person in New York to be cured of sickle cell anemia due to a genetic treatment called Lyfgenia.

Zynext Ventures is investing in Illexcor Therapeutics to advance the clinical development of ILX002, its lead candidate for ...

Doctors noticed that patients who had sickle cell anemia, a serious hereditary blood disease, were more likely to survive malaria, a disease which kills some 1.2 million people every year.

Sickle-cell anemia is due to a mutation in the gene encoding the β-subunit of hemoglobin (called HBB), which leads to an abnormal structure of the β-subunit protein chain and the sickle-cell ...

Sebastien Beauzile, 21, has been cured of sickle cell anemia, according to his doctors at Cohen Children’s Medical Center.

It started with the FDA approval for the first CRSPR-based gene therapy treatment for sickle cell anemia (SCA ... by a mutation in the hemoglobin gene (HBB). CRISPR-Cas9 acts as molecular scissors ...

On this map, the distribution of sickle-cell anemia haplotypes among nations with high prevalence of the disease are shown. Five distinct beta-globin haplotypes (indicated by colors) are found in ...

View Full Profile. Learn about our Editorial Policies. Today, the cause of sickle cell disease is well understood to be a point mutation in a hemoglobin gene called HBB that makes red blood cells grow ...

MONDAY, March 17, 2025 (HealthDay News) -- For 21 years, Sebastien Beauzile lived with the chronic pain of sickle cell anemia. Now, thanks to a groundbreaking genetic treatment, he is the first ...