In a previous animal study, scientists searched for the genetic culprits behind muscle weakening, but they used a single strain in order to limit unexplainable variation in the results. 3 “That’s like ...
Duchenne muscular dystrophy (DMD) is a genetic condition that causes progressive muscle weakness and wasting. It is an X-linked recessive disorder that occurs due to changes in the DMD gene ...
Research in the Leinwand lab focuses on unraveling mechanisms of genetic heart and skeletal muscle diseases using animal models, cell-culture systems and biophysical approaches. In addition to ...
Dyne Therapeutics started the new year with proof-of-concept clinical data for experimental genetic medicines addressing two rare muscle diseases—one of which has no FDA-approved treatments.