(NewsNation) — The FDA has approved the first gene therapy for metachromatic leukodystrophy (MLD), a rare and fatal disease primarily affecting children under the age of seven. The staggering ...

Genetics plays important role in when people first have sex, and when they have kids Jul 1, 2021 Scientists ID more than 1,200 genes linked to educational attainment ...

The new Kids First datasets advance our understanding of how genetics contribute to childhood cancers and congenital disorders, opening new doors for prevention and treatment.

Scientists at The Hospital for Sick Children (SickKids) have identified a key gene that could lead to next-generation treatments for medulloblastoma, the most common malignant brain tumor in children.

Gene therapy has allowed several children born with inherited deafness to hear. A small study published Wednesday documents significantly restored hearing in five of six kids treated in China.